A DocCheck channel. Curated by our expert Matthias Bastigkeit (specialist lecturer in pharmacology and medical journalist).
Leukemia, cystic fibrosis or tuberculosis – the diseases are rare, the affected patients not so much: approximately 4.3 million Germans suffer from an orphan disease. But the similarities stop at rareness, and thus doctors from all disciplines are confronted by them. Whether it’s autoimmune diseases, metabolic diseases, cancers or infectious diseases: they are treated with orphan drugs. In this channel, we fill the gaps in your knowledge of these niche drugs.